FULL DETAILS (Read-only)  -> Click Here to Create PDF for Current Dataset of Trial
CTRI Number  CTRI/2024/11/077478 [Registered on: 29/11/2024] Trial Registered Prospectively
Last Modified On: 05/12/2024
Post Graduate Thesis  No 
Type of Trial  Interventional 
Type of Study   Drug 
Study Design  Randomized, Parallel Group, Placebo Controlled Trial 
Public Title of Study   A Study to Investigate the Efficacy and Safety of Anifrolumab Administered as Subcutaneous Injection and Added to Standard of Care Compared with Placebo Added to Standard of Care in Adult Participants with Idiopathic Inflammatory Myopathies (Polymyositis and Dermatomyositis) 
Scientific Title of Study   A Multicenter, Parallel-group, Double-blind, 2-Arm, Phase III Study to Investigate the Efficacy and Safety of Anifrolumab Administered as Subcutaneous Injection and Added to Standard of Care Compared with Placebo Added to Standard of Care in Adult Participants with Idiopathic Inflammatory Myopathies (Polymyositis and Dermatomyositis) 
Trial Acronym  JASMINE 
Secondary IDs if Any  
Secondary ID  Identifier 
D3463C00003 V3.0 dated 06 March 2024  Protocol Number 
NCT06455449  ClinicalTrials.gov 
 
Details of Principal Investigator or overall Trial Coordinator (multi-center study)  
Name  Tapankumar M Shah  
Designation  Senior Director – Site Management and Monitoring, Biopharmaceuticals R&D 
Affiliation  AstraZeneca Pharma India Ltd. 
Address  Block N1, 12th Floor, Manyata Embassy Business Park, Rachenahalli, Outer Ring Road

Bangalore
KARNATAKA
560045
India 
Phone  9535104975  
Fax    
Email  tapankumar.shah@astrazeneca.com  
 
Details of Contact Person
Scientific Query
 
Name  Mr Tapankumar Shah 
Designation  Senior Director Asia Area Cluster Head SMM Country Head R and D Biopharmaceuticals 
Affiliation  AstraZeneca Pharma India Limited 
Address  AstraZeneca Pharma India Ltd, Block N1, 12th Floor, Manyata Embassy Business Park, Rachenahalli, Outer Ring Road

Bangalore
KARNATAKA
560045
India 
Phone  9535104975  
Fax    
Email  tapankumar.shah@astrazeneca.com  
 
Details of Contact Person
Public Query
 
Name  Mr Tapankumar Shah 
Designation  Senior Director Asia Area Cluster Head SMM Country Head R and D Biopharmaceuticals 
Affiliation  AstraZeneca Pharma India Limited 
Address  AstraZeneca Pharma India Ltd, Block N1, 12th Floor, Manyata Embassy Business Park, Rachenahalli, Outer Ring Road

Bangalore
KARNATAKA
560045
India 
Phone  9535104975  
Fax    
Email  tapankumar.shah@astrazeneca.com  
 
Source of Monetary or Material Support  
AstraZeneca AB, 151 85 Södertälje, Sweden 
 
Primary Sponsor  
Name  AstraZeneca AB 
Address  151 85 Södertälje, Sweden 
Type of Sponsor  Pharmaceutical industry-Global 
 
Details of Secondary Sponsor  
Name  Address 
AstraZeneca Pharma India Ltd  Block N1, 12th Floor, Manyata Embassy Business Park, Rachenahalli, Outer Ring Road, Bangalore - 560045, Karnataka, India 
 
Countries of Recruitment     Spain
Australia
Austria
Belgium
Brazil
Canada
China
Czech Republic
Denmark
France
Germany
Hungary
India
Israel
Italy
Japan
Mexico
Netherlands
Poland
Sweden
Taiwan
United Kingdom
United States of America
Bulgaria
Republic of Korea  
Sites of Study  
No of Sites = 9  
Name of Principal Investigator  Name of Site  Site Address  Phone/Fax/Email 
Dr Bhojani Kaushik Shashikant   Fortis Hospitals Limited, Mulund  Department of Rheumatology, Mulund Goregaon Link Road, Bhandup (W), PIN- 400078
Mumbai
MAHARASHTRA 
9619177718

kaushik.bhojani@fortishealthcare.com 
Dr Geetabali Sircar  IPGME&R and SSKM Hospital  244, Acharya J. C. Bose Road, Bhowanipore, Kolkata-700020
Kolkata
WEST BENGAL 
9433514259

geet4in@yahoo.co.in 
Dr Subramanian Ramaswamy  JSS Medical College,JSS Hospital  Sri Shivarathreeshwara Nagara,MG Road, Mysore- 570004
Mysore
KARNATAKA 
9945472441

Subsan05@gmail.com 
Dr Jyotsna Laxmikant Oak  Kokilaben Dhirubhai Ambani Hospital and Medical Research Institute  Rao Saheb Achutrao Patwardhan Marg, Four Bunglows, Andheri West, PIN - 400053
Mumbai
MAHARASHTRA 
9324717618

jyotsna.oak@kokilabenhospitals.com 
Dr Veeravalli Sarathchandra Mouli   Krishna Institute of Medical Sciences Limited  1-8-31/1, Minister Road, Secunderabad-500003
Hyderabad
TELANGANA 
9866000685

Sarath10@hotmail.com 
Dr Shahzeene Dhuria  Medanta Hospital, Lucknow  Sector-A, Pocket-1, Sushant Golf City, Amar Shaheed Path, PIN - 226030
Lucknow
UTTAR PRADESH 
9878229843

shahzeene.dhuria@gmail.com 
Dr Rajiva Gupta  Medanta The Medicity  Sector-38, Gurugram-122001, Haryana, India.
Gurgaon
HARYANA 
9810904592

Rajiva.gupta@medanta.org 
Dr Liza Rajasekhar   Nizams Institute of Medical Sciences  Department of Clinical Immunology and Rheumatology, Millenium block-04 floor, Punjagutta
Hyderabad
TELANGANA 
9391008618

lizarajasekhar@gmail.com 
Dr Dhaiwat Mrugeshbhai Shukla  Sheth Vadilal Sarabhai General Hospital  Madalpur Gam, Paldi Road, Ellisbridge, Ahmedabad-380006
Ahmadabad
GUJARAT 
8980024107

dr.dhaiwatshukla89@gmail.com 
 
Details of Ethics Committee  
No of Ethics Committees= 9  
Name of Committee  Approval Status 
Institutional Ethics Committee, Fortis Hospitals Limited, Mulund  Submittted/Under Review 
Institutional Ethics Committee, JSS Hospital  Approved 
Institutional Ethics Committee, Kokilaben Dhirubhai Ambani Hospital & Medical Research Institute  Submittted/Under Review 
Institutional Ethics Committee, Medanta Hospital, Lucknow  Submittted/Under Review 
IPGME and Research Oversight Committee  Approved 
KIMS Ethics Committee  Approved 
Medanta Institutional Ethics Committee  Approved 
NIMS Institutional Ethics Committee  Submittted/Under Review 
Sangini Hospital Ethics Committee, Sangini Hospital  Submittted/Under Review 
 
Regulatory Clearance Status from DCGI  
Status 
Approved/Obtained 
 
Health Condition / Problems Studied
Modification(s)  
Health Type  Condition 
Patients  (1) ICD-10 Condition: M332||Polymyositis, (2) ICD-10 Condition: M331||Other dermatomyositis,  
 
Intervention / Comparator Agent  
Type  Name  Details 
Intervention  Anifrolumab  Anifrolumab 120 mg/0.8 mL solution for injection in accessorized prefilled syringe (aPFS), QW, Subcutaneous (SC) injection, week 0 to week 52 (in double blind treatment period) and Week 52- Week 104 (open label treatment period) 
Comparator Agent  Placebo  Placebo solution for injection in aPFS, QW, Subcutaneous (SC) injection, week 0 to week 52 
 
Inclusion Criteria  
Age From  18.00 Year(s)
Age To  70.00 Year(s)
Gender  Both 
Details  1. Body weight ≥ 40 kg at screening
Disease Characteristics
Disease diagnosis, severity, and activity (inclusion criteria 2, 3, and 4 must be confirmed by the Disease Adjudication Committee.

2 Must have “probable” or “definite” diagnosis of PM according to the 2017 EULAR/ACR classification criteria for adult myositis (Lundberg et al 2017). Participants are eligible if:
a. Positive for anti-ARS antibodies or antibodies associated with OM by myositis autoantibody test performed at screening; or
b. Muscle biopsy performed during screening or the report of a muscle biopsy performed any time prior to signing the ICF that confirms this disease and excludes other types of myositis.
3. Must have moderate to severe PM at screening measured by having MMT-8 score of
≤ 136/150 PLUS at least 2 of the following:
a PGA ≥ 2.0 cm (VAS 10-cm scale).
b PtGA ≥ 2.0 cm (VAS 10-cm scale).
c HAQ-DI ≥ 0.25.
d One or more muscle enzyme elevation (CK, AST, ALT, aldolase, LDH)
≥ 1.3 × ULN.
e Global extra-muscular disease activity (MDAAT) ≥ 2.0 cm (VAS 10-cm scale).
4 Fulfill one of the following criteria of active disease at screening:
a Muscle enzyme elevation of CK ≥ 4 × ULN.
b Muscle enzyme elevation of CK ≥ 1 × ULN and < 4 × ULN with at least one of the following:
i. Report from MRI performed within 6 months prior to Day 1 (randomization) with evidence of muscle inflammation.
ii. Report from muscle biopsy performed within 6 months prior to Day 1 (randomization) that demonstrates active inflammation. Note: Results of muscle biopsy performed during screening may be used only if collected for inclusion 3(b). No muscular biopsy should be performed during screening for activity confirmation only.
iii. Report from electromyography performed within 6 months prior to Day 1 (randomization) that exhibits irritable myopathic pattern.
5 Currently receiving at least one of the following, unless the participant is intolerant to one or both (a) and (b), defined as the inability to continue treatment due to adverse effects, regardless of treatment dose:
a An oral prednisone dose of ≤ 20 mg/day (or prednisone equivalent) for a minimum of 2 weeks prior to signing the ICF and at a stable dose for a minimum of 4 weeks prior to Day 1 (randomization).
b Not more than one of the following medications administered for a minimum of 12 weeks prior to signing the ICF and at a stable dose for a minimum of 8 weeks prior to Day 1 (randomization):
i. Azathioprine ≤ 200 mg/day.
ii. Mycophenolate mofetil ≤ 3 g/day or mycophenolic acid ≤ 1.44 g/day.
iii. Methotrexate ≤ 25 mg/week oral, SC, or IM.
iv. Mizoribine ≤ 150 mg/day.
v. Tacrolimus ≤ 0.2 mg/kg/day; where local practice guidelines mandate or in case of safety concerns, monitoring of serum tacrolimus concentration may be performed at the discretion of investigator, with an aim of keeping a stable tacrolimus concentration targeting 5-10 ng/mL.
Cervical Cancer Screening
6 Females who have been or are sexually active with an intact cervix must have documentation of a cervical cancer screening (pap smear or HPV test as per local guidelines) with a normal test result within 2 years prior to Day 1 (randomization). Any abnormal cervical cancer screening result documented within 2 years prior to Day 1 (randomization) must be repeated to confirm eligibility. Note: Females < 25 years of age, who have never been sexually active or have well documented HPV vaccination records may not require a cervical cancer screening test.
Tuberculosis
7 Must meet all the following TB criteria:
a No medical history or signs or symptoms of active TB prior to or during the screening period.
b A chest CT scan obtained at screening with no evidence of active or signs of prior TB infection. If a CT scan cannot be performed during screening, a recent chest x-ray or CT scan performed within 12 weeks of screening, or a chest x-ray performed during the screening period may be acceptable.
c No recent contact with a person with active TB, or if there has been such contact, referral to a physician specializing in TB to undergo additional evaluation prior to Day 1 (randomization), documented comprehensively in source, and, if warranted, receipt of appropriate treatment for latent TB initiated before the first administration of study intervention.
d No history of latent TB prior to signing the ICF, except latent TB with documented completion of appropriate treatment.
8 Must undergo an IGRA test (eg, QFT-G test) for TB obtained from the central laboratory at screening with any of the following results:
a Negative test result.
b Positive test result: referral to a TB specialist for evaluation and for which active TB has been ruled out, and initiation of treatment for latent TB prior to the first administration of study intervention in accordance with local SoC.
c Indeterminate test result confirmed by repeat test using the same assay:
i. If in an endemic region, the participant must be referred to a TB specialist for evaluation (with assessment and treatment recommendation comprehensively documented in source) and initiation of appropriate latent TB treatment, if warranted, prior to the first administration of study intervention. If latent TB treatment is not warranted, the participant may enter the study. See
ii. If in a non-endemic region, the participant may enter the study without referral to a TB specialist and latent TB treatment. See Note: Endemic region is defined based on WHO lists of high burden countries for TB and multidrug-resistant TB (World Health Organization Global TB Report 2020)
Coronavirus Disease 2019
1 Any negative SARS-CoV-2 RT-PCR or antigen test result (central or local laboratory, as appropriate) as per local policies at screening, in addition to no known or suspected COVID-19 exposure within 2 weeks prior to signing the ICF based on the COVID-19 questionnaire. If there is a known or suspected exposure, the participant must be negative upon retest obtained after 2 weeks and must remain asymptomatic to be eligible for the study. Note: Participants positive at screening may be rescreened after 6 weeks of
mild/asymptomatic infections or at the discretion of the investigator, provided there has been no development of severe COVID-19 infection or sequelae. Participants may be rescreened a second time if the primary reason for screen failure was due to positive COVID-19 test.
Sex and Contraceptive/Barrier Requirements
Contraceptive use by participants should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies.

Female Participants:
2 Females of non-childbearing potential must be postmenopausal or have been surgically sterilized (eg, bilateral oophorectomy or complete hysterectomy), which should be documented in the participant’s medical records.
3 Females of childbearing potential:
a Must have a negative serum β-hCG test at screening.
b Must have a negative urine pregnancy test at randomization (Day 1), prior to administration of study intervention.
c Must use one highly effective method of contraception, plus a male condom, from screening until 16 weeks after the final dose of study intervention unless the participant is surgically sterile (eg, bilateral oophorectomy or complete hysterectomy), has a sterile/non-fertile male partner, is at least 12 months postmenopausal, or practices sustained abstinence consistent with the participant’s customary lifestyle.
 
 
ExclusionCriteria 
Details  1 Participants with documented DM, IBM, IMNM, juvenile myositis, drug-induced myositis, cancer-associated myositis (myositis diagnosed within 2 years of a diagnosis of cancer), and non-inflammatory myopathies (eg, muscular dystrophies).
a Participants with clinically significant fibromyalgia or with muscle symptoms that may interfere with study efficacy assessments in the opinion of the investigator are excluded.
2 Wheelchair-bound within 3 months prior to Day 1 (randomization) due to severe muscle involvement caused by PM.
3 Signs of severe uncontrolled extra-muscular disease damage related to PM as determined by any of the following:
a Interstitial lung disease that requires oxygen supplementation/therapy (of any type) or FVC < 55% of predicted.
b Severe cardiac manifestations such as congestive heart failure, arrhythmias, or conduction abnormalities requiring treatment, or myocardial infarction within 6 months prior to Day 1 (randomization).
c Severe dysphagia manifested as severely altered eating or swallowing, use of feeding tube or total parenteral nutrition, or hospitalization indicated.
4 Severe muscle damage in the opinion of the investigator or as per muscle MRI (if available).
5 Permanent weakness due to a non-PM cause (eg, stroke) in the opinion of the investigator.
6 History or evidence of suicidal ideation (severity of 4 [active: method and intent, but no plan] or 5 [active: method, intent, and plan]) within 6 months prior to signing the ICF, or any suicidal behavior within 12 months prior to signing the ICF or recurrent suicidal behavior in the lifetime of the participant based on an assessment with the C-SSRS at screening.
Infection and Malignancy Risk Factors
7 Any severe case, as defined by study guidelines, of herpes zoster infection at any time prior to Day 1 (randomization) including but not limited to:
a Non-cutaneous herpes, herpes encephalitis, or ophthalmic herpes involving the retina.
b Recurrent herpes zoster defined as 2 or more episodes within 2 years.
c Any herpes zoster infection that has not completely resolved within 12 weeks prior to signing the ICF.
8 History of cancer, apart from:
a Squamous or basal cell carcinoma of the skin treated with documented success of curative therapy ≥ 3 months prior to Day 1 (randomization)
b Cervical cancer in situ treated with apparent success with curative therapy ≥ 1 year prior to Day 1 (randomization).
9 Known history of a primary immunodeficiency, splenectomy, or any underlying condition that predisposes the participant to infection.
10 Positive test result for HIV antibody or infection (ie, positive nucleic acid test) by central laboratory at screening.
11 Positive test result for hepatitis B serology, as confirmed by central laboratory at screening for:
a Hepatitis B surface antigen; or
b Hepatitis B core antibody and HBV DNA detected above the LLOQ by reflex testing. Note: Participants who are positive for hepatitis B core antibody at screening will be tested every 12 to 16 weeks (Table 2) for HBV DNA. To remain eligible for the study, the participant’s HBV DNA levels must remain below the LLOQ as per the central laboratory. See Appendix M for Japan.
12 Active hepatitis C infection, defined as positive HCV antibody and detectable HCV RNA, as confirmed by central laboratory at screening. Participants with positive anti-HCV antibodies can be eligible if HCV-RNA is undetectable at screening and remains undetectable during study (test will be repeated every 24 to 28 weeks [Table 2]).
13 Any clinical cytomegalovirus or Epstein-Barr virus infection that has not completely resolved within 12 weeks prior to signing the ICF.
14 Opportunistic infection (Section 8.4.4.3) requiring hospitalization or IV antimicrobial treatment within 3 years prior to Day 1 (randomization).
15 Clinically significant chronic infection (eg, osteomyelitis, bronchiectasis, etc) within 8 weeks prior to signing the ICF (chronic nail infections are allowed).
16 Any infection requiring hospitalization or treatment with IV anti-infective medications not completed at least 4 weeks prior to signing the ICF.
17 Any infection requiring oral anti-infective medications (including antivirals) within 2 weeks prior to Day 1 (randomization).
18 Must not meet any of the following COVID-19 infection criteria:
a Any history of severe COVID-19 infection (eg, prolonged hospitalization [hospitalization for observational purposes is not exclusionary]) or any prior COVID-19 infection with documented long COVID and/or clinically significant unresolved sequelae.
b Any mild/asymptomatic COVID-19 infection (laboratory confirmed or suspected based on clinical symptoms) within 6 weeks prior to Day 1 (randomization).
Hypersensitivity, Including Anaphylaxis
19 Known history of allergy or reaction to any component of the study intervention formulation or history of anaphylaxis to any human gamma globulin therapy.
20 Any history of an anaphylactic reaction to human proteins or mAbs.
Prior/Concomitant Therapy
21 Prior receipt of anifrolumab.
22 Any change in route of administration of oral, SC, or IM methotrexate anytime within 8 weeks prior to signing the ICF through Day 1 (randomization).
23 Receipt of any commercially available biologic agent within 5 half-lives (see Appendix H for a complete list) prior to signing the ICF.
24 Receipt of any of the prohibited medications listed in Appendix H if the required discontinuation or washout time prior to signing the ICF is not met:
a B cell depleting therapy (eg, rituximab) within 26 weeks prior to signing the ICF or if administered more than 26 weeks prior to signing the ICF, absolute B cell count below lower limit of normal or below baseline value prior to receipt of B cell- depleting therapy (whichever is lower).
25 Receipt of any of the following:
a Intra-articular, IM, or IV glucocorticosteroids within 4 weeks prior to Day 1 (randomization).
b Any live or attenuated vaccine within 8 weeks prior to signing the ICF. Note: Administration of killed vaccines is acceptable. The sponsor recommends the
investigators ensure that the participant is up to date on vaccinations, including COVID-19, pneumonia, varicella zoster, and influenza (inactivated/recombinant) vaccines prior to screening.
c Blood transfusion or receipt of blood products within 4 weeks prior to signing the ICF.
26 Cannabinoid use that is not at a stable regimen for at least 8 weeks prior to signing the ICF. Any new medicinal cannabinoid should not be started during the study
(Section 6.9.4)
Prior/Concurrent Clinical Study Experience
27 Receipt of > 2 investigational products for the disease under study (PM) since time of diagnosis and through signing the ICF.
28 Receipt of any investigational product (small molecule or biologic agent), including licensed drugs that are not approved for the treatment of myositis (Appendix H), within 4 weeks or 5 half-lives prior to signing the ICF, whichever is longer.
29 Concurrent enrollment in another clinical study with an investigational product.
 
 
Method of Generating Random Sequence    
Method of Concealment    
Blinding/Masking    
Primary Outcome  
Outcome  TimePoints 
To demonstrate the superiority of anifrolumab to placebo on moderate improvement in disease activity at Week 24  Participants who have at least moderate improvement in disease activity TIS ≥ 40 at Week 52, where a responder (yes/no) for moderate improvement is defined as a participant who meets the following criteria:
- TIS ≥ 40 points at Week 52 and
- Has not met “confirmed deterioration” criteria at 2 consecutive visits up to and including Week 52
 
 
Secondary Outcome  
Outcome  TimePoints 
To demonstrate the superiority of anifrolumab to placebo on muscle improvement at Week 52  MMT-8 (CSM) change from baseline at Week 52 
To demonstrate the superiority of anifrolumab to placebo on OCS dose reduction at Week 52  Participants who achieve OCS dose ≤ 7.5 mg/day at Week 52 (yes/no).
Only participants with baseline OCS dose 7.5 mg/day at baseline will be included in the analysis.
 
To demonstrate the superiority of anifrolumab to placebo on moderate improvement in disease activity in PM participants at Week 52  Participants who have at least moderate improvement in disease activity TIS ≥ 40 at Week 52, where a responder (yes/no) for moderate improvement is defined as a participant who meets the following criteria:
- TIS ≥ 40 points at Week 52 and
- Has not met “confirmed deterioration” criteria at 2 consecutive visits up to & including Week 52
Only PM participants will be included in the analysis.
 
To demonstrate the superiority of anifrolumab to placebo on moderate improvement in disease activity in DM participants at Week 52  Participants who have at least moderate improvement in disease activity TIS ≥ 40 at Week 52, where a responder (yes/no) for moderate improvement is defined as a participant who meets the following criteria:
- TIS ≥ 40 points at Week 52 and
- Has not met “confirmed deterioration” criteria at 2 consecutive visits up to & including Week 52
Only DM participants will be included in the analysis.
 
To demonstrate the superiority of anifrolumab to placebo on improving skin activity at Week 8  CDASI-activity change from baseline at Week 8.
Only DM participants with CDASI-activity 14 at baseline will be included in the analysis.
 
To assess the efficacy of anifrolumab compared with placebo on disease activity at Week 52  Change from baseline at Week 52 in CSMs:
- PGA
- PtGA
- Muscle enzymes
- MDAAT extra-muscular disease activity
- HAQ-DI
 
To assess the efficacy of anifrolumab compared with placebo on cutaneous dermatomyositis activity investigator global assessment   - Participants who achieve CDA-IGA score ≤ 1 at Week 8 (yes/no)
- Participants who achieve CDA-IGA score ≤ 1 at Week 24 (yes/no)
- Participants who achieve CDA-IGA score ≤ 1 at Week 52 (yes/no)
Only DM participants with CDA-IGA ≥ 2 at baseline will be included in the analysis of these endpoints.
 
To assess the efficacy of anifrolumab compared with placebo on 5-D itch  - 5-D itch change from baseline at Week 8
- 5-D itch change from baseline at Week 24
- 5-D itch change from baseline at Week 52
Only DM participants with CDASI-activity 14 at baseline will be included in the analysis of these endpoints.
 
To assess the efficacy of anifrolumab compared with placebo on early onset of action on minimal improvement in disease activity at Week 8  Participants who have at least minimal improvement in disease activity TIS ≥ 20 at Week 8, where a responder (yes/no) for minimal improvement is defined as a participant who meets the following criteria:
- TIS ≥ 20 points at Week 8 and
- Has not met “confirmed deterioration” criteria at 2 consecutive visits up to & including Week 8
 
To assess the efficacy of anifrolumab compared with placebo on cumulative corticosteroid dose  - Cumulative corticosteroids use as determined by the normalized standardized AUC from baseline up to & including Week 24
- Cumulative corticosteroids use as determined by the normalized standardized AUC from baseline up to & including Week 52
 
To assess the efficacy of anifrolumab compared with placebo on major improvement in disease activity at Week 52  Participants who have major improvement in disease activity TIS ≥ 60 at Week 52, where a responder (yes/no) for major improvement is defined as a participant who meets the following criteria:
- TIS ≥ 60 points at Week 52 and
- Has not met “confirmed deterioration” criteria at 2 consecutive visits up to & including Week 52
 
To assess the safety & tolerability of anifrolumab compared with placebo  Safety & tolerability will be evaluated in terms of AEs, vital signs, clinical laboratory tests, 12-lead ECGs, physical examination, & C SSRS.
The AESIs are:
- Serious non-opportunistic infection
- Opportunistic infection
- Herpes zoster
- Tuberculosis including latent tuberculosis
 
To assess the safety & tolerability anifrolumab compared with placebo  Safety & tolerability will be evaluated in terms of AEs, vital signs, clinical laboratory tests, 12-lead ECGs, physical examination, & C SSRS.
The AESIs are:
- Malignancy
- Injection site reaction
- Major adverse cardiovascular events
Assessments of AEs, SAEs, & AESIs will also be collected during the safety Follow-up Period (12 weeks from Week 52/EDV-DB or Week 104/EDV-OL). 
 
Target Sample Size   Total Sample Size="162"
Sample Size from India="20" 
Final Enrollment numbers achieved (Total)= "Applicable only for Completed/Terminated trials"
Final Enrollment numbers achieved (India)="Applicable only for Completed/Terminated trials" 
Phase of Trial   Phase 3 
Date of First Enrollment (India)   09/12/2024 
Date of Study Completion (India) Applicable only for Completed/Terminated trials 
Date of First Enrollment (Global)  27/09/2023 
Date of Study Completion (Global) Applicable only for Completed/Terminated trials 
Estimated Duration of Trial   Years="3"
Months="0"
Days="0" 
Recruitment Status of Trial (Global)   Open to Recruitment 
Recruitment Status of Trial (India)  Not Yet Recruiting 
Publication Details   N/A 
Individual Participant Data (IPD) Sharing Statement

Will individual participant data (IPD) be shared publicly (including data dictionaries)?  

Response - NO
Brief Summary  

This is a multicentre, randomized, double-blind, placebo-controlled, Phase III study to evaluate the efficacy and safety of anifrolumab in adult participants with moderate to severe active Polymyositis (PM), while receiving stable standard-of-care therapy. The study design includes a double-blind, placebo-controlled treatment period of 24 weeks; 162 eligible participants will be randomized in a 1:1 ratio to receive anifrolumab 120 mg SC QW or placebo SC QW for 24 weeks (Week 0 Day 1 to Week 23 Day 162). At Week 24, all participants will rollover to an open-label period of 28 weeks in which they will receive anifrolumab 120 mg SC QW.

 

The study intervention (anifrolumab or placebo) will be administered on top of standard of care treatments, which are allowed at stable regimens and doses as per the specifications described in Section 6.9.2 of the Clinical Study Protocol. To

minimize the risk of baseline imbalances between anifrolumab and placebo for potentially confounding variables, the randomization will be stratified on the following factors at baseline: anti-ARS antibodies or antibodies associated with overlap myositis by myositis autoantibody test (positive versus negative); MMT-8 (< 125/150 versus ≥ 125/150); and oral prednisone dose (< 10 mg/day versus ≥ 10 mg/day). To be eligible for the study, participants must have moderate to severe active PM and be receiving SoC with oral corticosteroid and/or immunosuppressant therapy. Since no biological or small-molecule therapy is currently approved specifically in Polymyositis, it is assumed that the placebo group’s treatment corresponds to the current accepted standard of care. The use of placebo for 24 weeks is considered the minimal duration to allow for a proper double-blinded treatment period and the unbiased assessment of the efficacy and safety of Anifrolumab necessary for a registrational Phase 3 study in PM. Assessment of long-term efficacy and safety beyond Week 24 up to Week 52 will be possible, but with all participants receiving Anifrolumab 
Close